MBOAT4/GOAT Drug Discovery Landscape & Assay Solutions

Subtitle: Market Intelligence, Clinical Progress, and High-Purity Reagents for Metabolic Disease Development.

TarMart Solution Ecosystem & Related Targets

Comprehensive reagent toolkit for MBOAT4 drug discovery. Select your modality below:

Component / Network Product Description Product Link
Gene Delivery MBOAT4 Lentivirus Premade Particles
Full-length human ORF (codon-optimized), CMV promoter, Puromycin selection, HEK293 packaged. Titer >1x10^8 TU/mL. Also available as Promise-ORF/Lentivirus for stable cell line generation.
View MBOAT4 Products
Membrane Assay System MBOAT4 Stable Cell Line Lysate
HEK293 cells stably expressing human MBOAT4, membrane fraction purified, Endotoxin <1EU/mg. Sequence Verified.
View MBOAT4 Products
Benchmark Ab Anti-MBOAT4 Recombinant Positive Control Antibody (Clone 4C11)
Mouse monoclonal IgG, C-terminal epitope, validated for Western and IP. High Purity (>95%).
View MBOAT4 Products
Validator MBOAT4 siRNA Set (3 unique targets)
For knockdown verification and specificity controls. HPLC purified.
View MBOAT4 Products
Substrate Control Ghrelin (Active Form)
Human ghrelin (1-28), Octanoylated, Synthetic. High Purity (>95%). For enzymatic assays.
View Ghrelin Products
Pathway Partner GHSR (Growth Hormone Secretagogue Receptor)
Full-length lentivirus for functional signaling assays (calcium flux).
View GHSR Products
Selectivity Control MBOAT2 (Lysophospholipid Acyltransferase)
Recombinant membrane preparation for counter-screening off-target effects.
View MBOAT2 Products

Critical Assay Challenge vs TarMart Advantage

Critical Assay Challenge The TarMart Advantage (Technical Spec)
Multi-pass membrane topology preservation for enzymatic activity Lentivirus-transduced HEK293 cells expressing native conformation MBOAT4 with correct membrane insertion verified by flow cytometry
Substrate (Ghrelin) co-expression for octanoylation assays Dual-promoter lentivirus or co-transfection system available with Ghrelin ORF (View Ghrelin Products)
MBOAT family selectivity screening (MBOAT1/2/7) Ortholog and paralog membrane protein panel (Human/Mouse/Cyno) with sequence identity verified by mass spec
Catalytic dead controls for assay validation Site-directed mutant lentivirus available (H338A catalytic dead), Sequence Verified
Cross-species translation (rodent to primate) Human, Mouse, Rat, and Cynomolgus MBOAT4 lentivirus with conserved active site alignment
Lack of Controls / False Positives Recombinant positive control antibodies and validated siRNA included for specificity checks.

Live MBOAT4 R&D Tracker

Market data changes daily. Access the latest global pipeline status directly:

Global Clinical Landscape & Future Outlook

The race for MBOAT4/GOAT therapeutics is intensifying. As a critical enzyme activating ghrelin, inhibiting MBOAT4 presents a promising pathway for treating obesity, diabetes, and Prader-Willi syndrome. Major players are shifting focus from traditional enzyme kinetics to cell-based inhibitor screening and brain-penetrant small molecules. First-generation peripheral inhibitors show promise, while next-wave R&D targets central nervous system penetration for appetite control and oncology applications where ghrelin signaling promotes tumor proliferation. Future trends point towards combining MBOAT4 inhibitors with GLP-1 agonists to maximize weight loss and metabolic control.

Competitive Modality & Indication Snapshot

Modality Representative Players Key Indications Critical Assay Need (Why TarMart?)
Small Molecule Inhibitor Academic consortia, Early-stage Biotech Obesity, Type 2 Diabetes Membrane-based Enzymatic Assay (Need intact MBOAT4 expressing cells)
Peptide Inhibitor (e.g., GO-CoA-Tat) Research Institutions Metabolic Syndrome Cell Permeability & Internalization Assay
Antisense Oligonucleotide Specialized Genetic Medicine Firms NAFLD/NASH Gene Knockdown Validation (Need siRNA controls)
Dual Ghrelin/GHSR Modulators Metabolic Disease Focused Biotechs Cancer Cachexia Pathway Integration Assay (MBOAT4 + GHSR co-expression)

Key Genetic Variants

Key mutations in MBOAT4 (UniProt Q96T53):

  • rs7813902: Does not affect octanoyltransferase activity (evidence: UniProt VAR_059434).
  • rs16876563: Documented variant (evidence: UniProt VAR_030069). These variants are useful for designing negative controls and assessing drug resistance profiles.